Craig Mayer, Nick WIlliams, Vojtech Huser
Lister Hill National Center for Biomedical Communications, National Library of Medicine, NIH, Bethesda, MD

See the full regCTG repository at https://github.com/lhncbc/CRI/tree/master/regCTG

To return to the list of conditions and view other reports go to https://lhncbc.github.io/CRI/regCTG/regCTG-condition_report_links.html


Study Counts

Type Study_count
Total_Studies 921
interventional 674
Observational 240
Registry 7

Studies over Time by Start Date

```

Interventional Trials

Intervention Type

intervention_type Study_Count
Drug 251
Drug|placebo 171
Other 69
Behavioral 37
Device 36
Dietary Supplement 19
Procedure 16
Dietary Supplement|placebo 15
Device|Other 9
Diagnostic Test 7
Device|Drug 6
Biological|placebo 5
Biological 4
Genetic 4
Drug|Other 3
Other|Procedure 3
Behavioral|Drug 2
Device|placebo 2
Device|Procedure 2
Dietary Supplement|Drug 2
Behavioral|Device 1
Behavioral|Dietary Supplement 1
Behavioral|Other 1
Biological|Diagnostic Test|Other 1
Device|Diagnostic Test|Other 1
Diagnostic Test|Drug|Other 1
Dietary Supplement|Other|Procedure 1
Drug|Procedure 1
placebo 1
placebo|Procedure 1
Radiation 1

Count of Studies by Intervention (normalized and mapped)

Interventions over Time

Yearly studies for each intervention by start date

Studies by Country

Country Study_Count
United States 239
NA 48
United Kingdom 46
France 44
Canada 30
Belgium 19
Germany 17
United States|Canada 17
Australia 12
Israel 10
Italy 10
Spain 9
Turkey 6
Brazil 5
Sweden 5
Netherlands 4
Switzerland 4
United States|Australia|Canada|Denmark|Germany|Ireland|Israel|Poland|Spain|Switzerland|United Kingdom 3
United States|Australia|Canada|New Zealand 3
United States|Canada|United Kingdom 3
Australia|New Zealand 2
Australia|United Kingdom 2
Belgium|Hungary|North Macedonia|Poland|Serbia|Slovakia|Ukraine 2
Egypt 2
Germany|United Kingdom 2
Poland 2
United States|Australia|Austria|Belgium|Canada|Czechia|France|Germany|Greece|Italy|Netherlands|Sweden|United Kingdom 2
United States|Australia|Belgium|Canada|Denmark|France|Germany|Sweden|United Kingdom 2
United States|Australia|Canada 2
United States|Australia|Canada|Czech Republic|France|Germany|Ireland|United Kingdom 2
United States|Australia|Canada|Ireland|United Kingdom 2
United States|Belgium|Canada|France|Germany|Israel|Italy|Netherlands|Spain|Sweden|United Kingdom 2
United States|Belgium|France 2
Argentina|Canada 1
Australia|Belgium|Czechia|Germany|Ireland|United Kingdom 1
Australia|Belgium|Denmark|France|Germany|Ireland|Poland|Switzerland|United Kingdom 1
Australia|Belgium|Germany|United Kingdom 1
Australia|Czech Republic|Germany|Ireland|United Kingdom 1
Australia|Czechia|Germany|United Kingdom 1
Australia|Ireland|United Kingdom 1
Austria 1
Austria|Belgium|Bulgaria|Canada|Denmark|France|Germany|Greece|Hungary|Ireland|Italy|Netherlands|Poland|Serbia|Slovakia|Spain|Sweden|United Kingdom 1
Austria|Belgium|Germany|Hungary|Ireland|Italy|Poland|Spain|Sweden 1
Austria|France|Germany|Italy 1
Belgium|Bulgaria|France|Germany|Italy|Poland|United Kingdom 1
Belgium|Bulgaria|Germany|Greece|Netherlands|Serbia|Sweden|United Kingdom 1
Belgium|Netherlands 1
Bulgaria|Canada|Denmark|France|Germany|Greece|Hungary|Ireland|Italy|Netherlands|Poland|Serbia|Belgium|Austria|Slovakia|Spain|United Kingdom 1
Bulgaria|Egypt|Estonia|India|Latvia|Lithuania|Romania|Russian Federation|South Africa 1
Bulgaria|Estonia|Latvia|Lithuania|Romania|Russian Federation|South Africa 1
Bulgaria|Hungary|Poland|United Kingdom 1
Canada|Egypt|France|Germany|Greece|Hungary|Italy|Romania|Russian Federation|Switzerland 1
Canada|France|Italy|Portugal|United Kingdom 1
Canada|France|United States|Australia|Austria|Israel|Spain 1
Cuba 1
Czech Republic|Hungary|Poland|Spain 1
Czech Republic|Moldova, Republic of|Slovakia 1
Czech Republic|Slovakia 1
Czechia|France|Germany|Hungary|Poland|Russian Federation|Spain|Ukraine 1
Denmark 1
Denmark|Germany|Norway|Sweden|United Kingdom 1
Denmark|Germany|Poland|Russian Federation|Sweden|United Kingdom 1
Denmark|Norway|Sweden 1
Estonia|Russian Federation 1
France|Belgium 1
France|Poland|Ukraine 1
France|United Kingdom 1
France|United States|Austria|Belgium|Denmark|Germany|Ireland|Italy|Netherlands|Portugal|Spain|Switzerland|United Kingdom 1
France|United States|Belgium|Canada|Czechia|Hungary|Netherlands|Serbia|Slovakia|Spain|United Kingdom 1
Germany|Ireland|Spain|Switzerland|United Kingdom 1
Germany|Israel 1
Germany|Netherlands 1
Germany|Poland 1
Germany|Switzerland 1
Germany|United States|Australia|Belgium|Canada|Denmark|France|New Zealand|United Kingdom 1
Holy See (Vatican City State)|Italy 1
Hungary 1
Hungary|Spain 1
India 1
Ireland 1
Ireland|Italy|Germany|United States|Australia|Austria|Belgium|Canada|France|United Kingdom 1
Ireland|United Kingdom 1
Ireland|United States|Australia|Belgium|Canada|Denmark|France|Germany|Italy|Netherlands|Spain|United Kingdom 1
Ireland|United States|Australia|United Kingdom 1
Italy|United States|Argentina|Australia|Belgium|Brazil|Bulgaria|Canada|France|Germany|Greece|Israel|Netherlands|Poland|Spain|United Kingdom 1
Italy|United States|Australia|Austria|Belgium|Canada|Denmark|France|Germany|Ireland|Israel|Netherlands|Spain|Sweden|Switzerland|United Kingdom 1
Netherlands|Poland 1
Netherlands|United Kingdom 1
Norway 1
Peru|Spain 1
United States|Argentina|Australia|Belgium|Canada|Czechia|Hungary|Israel|Italy|Mexico|New Zealand|Poland|Romania|Russian Federation|Slovakia|South Africa|Spain|Ukraine 1
United States|Argentina|Australia|Canada|France|Germany|Hungary|Italy|Mexico|Spain 1
United States|Argentina|Belgium|Canada|France|Germany|Netherlands 1
United States|Australia|Austria|Belgium|Canada|Czech Republic|Denmark|France|Germany|Ireland|Italy|Netherlands|Spain|Sweden|United Kingdom 1
United States|Australia|Austria|Belgium|Canada|Czech Republic|France|Germany|Hungary|Ireland|Israel|Italy|Poland|Portugal|Russian Federation|Slovakia|South Africa|Spain|Switzerland|United Kingdom 1
United States|Australia|Austria|Belgium|Canada|Denmark|France|Germany|Spain|United Kingdom 1
United States|Australia|Austria|Belgium|Canada|Denmark|Germany|Italy|Spain|United Kingdom 1
United States|Australia|Austria|Canada 1
United States|Australia|Belgium|Canada|Denmark|France|Germany|Ireland|Israel|Italy|Netherlands|Spain|United Kingdom 1
United States|Australia|Belgium|Canada|Denmark|France|Germany|Ireland|Poland|Switzerland|United Kingdom 1
United States|Australia|Belgium|Canada|Denmark|France|Italy|Netherlands|Spain 1
United States|Australia|Belgium|Canada|France|Germany|Israel|Italy|Netherlands|Switzerland|United Kingdom 1
United States|Australia|Belgium|France|Germany|Italy|Netherlands|New Zealand|Portugal|Russian Federation|United Kingdom 1
United States|Australia|Belgium|France|Germany|New Zealand|United Kingdom 1
United States|Australia|Belgium|Germany|Ireland|Netherlands|United Kingdom 1
United States|Australia|Belgium|Netherlands 1
United States|Australia|Canada|Chile|Colombia|France|Germany|Hungary|Israel|Italy|Mexico|Netherlands|Spain|United Kingdom 1
United States|Australia|Canada|Czech Republic|France|Germany|Ireland|Italy|Netherlands|Sweden|United Kingdom 1
United States|Australia|Canada|Denmark|Germany|Israel|Norway|Sweden|United Kingdom 1
United States|Australia|Canada|France|Germany|Ireland|United Kingdom 1
United States|Australia|Canada|Germany|Ireland|United Kingdom 1
United States|Australia|Canada|Israel|New Zealand 1
United States|Australia|Germany|Ireland|Spain|United Kingdom 1
United States|Australia|Israel|New Zealand 1
United States|Austria|Belgium|Bulgaria|Canada|Czechia|France|Germany|Greece|Hungary|Italy|Netherlands|Poland|Portugal|Romania|Russian Federation|Serbia|Slovakia|Spain|Sweden|United Kingdom 1
United States|Austria|Belgium|Denmark|France|Germany|Greece|Israel|Italy|Netherlands|Spain|United Kingdom 1
United States|Austria|Belgium|France|Germany|Italy|Netherlands|Poland|Spain 1
United States|Austria|Canada|France|Germany|Netherlands|Switzerland|United Kingdom 1
United States|Belgium|Canada|Czechia|Denmark|France|Germany|Italy|Spain|United Kingdom 1
United States|Belgium|Canada|France|Germany|Italy|United Kingdom 1
United States|Belgium|Canada|Germany|Netherlands 1
United States|Belgium|France|Germany|Italy|Poland|United Kingdom 1
United States|Belgium|France|United Kingdom 1
United States|Belgium|Netherlands|Serbia|Spain|United Kingdom 1
United States|Belgium|Netherlands|United Kingdom 1
United States|Canada|Czechia|Hungary|Israel|Poland|Spain 1
United States|Canada|Denmark|France|Germany 1
United States|Canada|Denmark|France|Germany|Ireland|Italy|Netherlands|Spain|Sweden|Switzerland|United Kingdom 1
United States|Canada|Denmark|Germany|Sweden 1
United States|Canada|France|Germany|Israel 1
United States|Canada|Germany 1
United States|Canada|Germany|United Kingdom 1
United States|Czechia|Hungary|Israel|Poland|Spain 1
United States|France|Germany 1
United States|France|Germany|Ireland|Israel|United Kingdom 1
United States|France|Germany|Italy|Poland|Spain 1
United States|France|Ireland|United Kingdom 1
United States|Germany 1
United States|Germany|Netherlands 1
United States|Germany|Netherlands|Portugal|United Kingdom 1
United States|Hungary|Israel|South Africa|Spain 1
United States|Ireland|Israel|United Kingdom 1
United States|Italy 1
United States|Italy|United Kingdom 1
United States|Poland 1
United States|Spain 1
United States|United Kingdom 1

Sites per Study

Site_count Study_Count
1 376
2 40
3 21
4 16
5 16
6 9
7 8
8 7
9 8
10 4
11 8
12 5
13 4
14 6
15 6
16 5
17 6
18 3
19 5
20 7
21 3
22 1
23 5
24 2
25 4
26 2
27 4
28 2
29 6
30 2
31 2
33 3
35 2
36 3
37 1
38 5
39 2
40 5
42 1
43 1
44 2
45 1
46 2
47 1
48 2
49 1
50 2
53 4
54 3
55 1
56 3
58 3
61 1
62 1
65 2
67 1
68 1
71 2
72 1
75 2
82 1
84 1
86 1
88 1
90 1
92 1
93 1
94 1
97 1
99 1
100 2
101 1
106 1
107 1
109 1
110 1
112 1
115 1
130 1
159 1
167 1

Phase

Phase Study_Count
N/A 221
Phase 2 132
Phase 3 123
Phase 1 95
Phase 4 52
Phase 1/Phase 2 37
Early Phase 1 8
Phase 2/Phase 3 6

Number of Arms

Number_of_Arms Count_of_Studies
1 160
2 321
3 62
4 34
5 8
6 11
7 2
8 3
9 1
10 2
12 1
13 1
15 2
16 1
22 1
NA 64

Enrollment Metrics by Phase

Measure Early.Phase.1 N.A Phase.1 Phase.1.Phase.2 Phase.2 Phase.2.Phase.3 Phase.3 Phase.4
Min. 7.000 3.00000 5.00000 9.00000 6.00000 16 2.0000 1.00000
1st Qu. 14.000 21.00000 12.00000 17.00000 20.00000 40 49.0000 15.75000
Median 31.000 37.00000 20.00000 36.00000 40.00000 60 113.0000 26.00000
Mean 41.125 76.30137 32.88421 48.56757 69.51908 62 175.6529 73.46154
3rd Qu. 47.500 70.00000 34.50000 63.00000 92.00000 80 223.0000 61.75000
Max. 136.000 3600.00000 200.00000 230.00000 510.00000 116 1164.0000 1048.00000

Trial Group Type

group_type Group_Count
Experimental 796
Active Comparator 237
Placebo Comparator 233
Other 71
NA 64
No Intervention 46
Sham Comparator 7

Intervention Model

intervention_model Study_Count
Parallel Assignment 303
Single Group Assignment 205
Crossover Assignment 128
NA 21
Sequential Assignment 15
Factorial Assignment 2

Primary Purpose

primary_purpose Study_Count
Treatment 479
Diagnostic 35
Basic Science 34
Other 32
Prevention 29
Supportive Care 27
NA 18
Health Services Research 12
Screening 7
Educational/Counseling/Training 1

Observational Studies

Studies by Country

Country Study_Count
United States 109
France 37
NA 14
United Kingdom 14
Canada 10
Germany 8
Belgium 5
Turkey 5
Italy 4
Netherlands 4
Switzerland 4
Israel 3
Spain 3
United States|Canada 3
Austria|Germany 2
Korea, Republic of 2
Australia 1
Belgium|Netherlands 1
Brazil 1
Czechia 1
Denmark 1
Germany|Netherlands 1
India|Sri Lanka 1
Italy|Netherlands|United Kingdom 1
Japan 1
Norway 1
Qatar 1
Sweden 1
United States|Australia 1

Sites per Study

Site_count Study_Count
1 184
2 8
3 12
4 7
5 1
6 3
7 4
8 2
9 1
10 2
11 1
12 1
13 1
15 1
17 1
26 1
28 1
31 1
36 1
38 2
47 1
52 1
54 1
56 1
123 1

Enrollment Metrics

Measure Observational
Min 0.0000
1st Qu 38.0000
Median 76.0000
Mean 875.2353
3rd Qu 178.7500
Max 120000.0000

Observation Model

observational_model Study_Count
Cohort 136
Case-Only 32
Case-Control 27
NA 17
Case Control 12
Other 9
Family-Based 4
Case-Crossover 1
Defined Population 1
Defined Population, Natural History 1

Time Perspective

time_perspective Study_Count
Prospective 166
Cross-Sectional 35
Retrospective 22
Other 6
NA 6
Cross-Sectional, Prospective 3
Longitudinal 1
Longitudinal, Prospective 1

Registries

Studies by Country

Country Study_Count
Belgium 1
Israel 1
Korea, Republic of 1
Netherlands 1
Turkey 1
United Kingdom 1
United States 1

Sites per Study

Site_count Study_Count
1 6
47 1

Enrollment Metrics

Measure Registries
Min 20.0000
1st Qu 45.0000
Median 60.0000
Mean 102.8571
3rd Qu 145.0000
Max 260.0000

Registry Model

observational_model Study_Count
Cohort 4
Case-Control 1
Family-Based 1
Other 1

Time Perspective

time_perspective Study_Count
Prospective 5
Cross-Sectional 2

Follow-up

target_duration Study_Count
5 Years 2
1 Day 1
1 Year 1
2 Years 1
3 Years 1
6 Months 1

Overview of Studies

Interventional Trials

#If less then 500 trials

Observational Studiess

#If less then 500 studies

nct_id brief_title link overall_status source primary_completion_date
NCT03390985 Canadian Observation Trial in CF Patients Undergoing Treatment With Ivacaftor https://ClinicalTrials.gov/show/NCT03390985 Completed The Hospital for Sick Children 2017-07-26
NCT03381157 Fidgety Movements in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT03381157 Completed Hacettepe University 2019-02-02
NCT03377686 Breath Analysis in Children by New Point-of-care Instruments https://ClinicalTrials.gov/show/NCT03377686 Completed Maastricht University Medical Center 2017-11-30
NCT03577756 Neurodevelopmental Assessment of Infants With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT03577756 Recruiting Hacettepe University 2019-12-12
NCT03820752 Vaccination Coverage and Level of Protection in Patients at Risk https://ClinicalTrials.gov/show/NCT03820752 Recruiting Universitaire Ziekenhuizen Leuven 2017-06-30
NCT03820349 Cystic Fibrosis and Cognitive Function https://ClinicalTrials.gov/show/NCT03820349 Recruiting University of Minnesota 2021-04-30
NCT03338595 Longitudinal Assessment of Exercise Capacity and Vascular Function in Patients With CF https://ClinicalTrials.gov/show/NCT03338595 Active, not recruiting Augusta University 2020-05-31
NCT03335202 Longitudinal Analysis of Respiratory and Intestinal Microbiome in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT03335202 Recruiting University of Kiel 2019-09-30
NCT03323983 Exploratory Study on Link Between Dynamic Hyperinflation and Lung Clearance Index in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT03323983 Completed Centre Hospitalier Universitaire de Besancon 2016-11-30
NCT03320382 Multiple Breath Washout, a Clinimetric Dataset https://ClinicalTrials.gov/show/NCT03320382 Recruiting Imperial College London 2021-03-31
NCT03318328 Evaluation of Food Insecurity in Adults and Children With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT03318328 Completed St. Luke’s Health System, Boise, Idaho 2015-03-31
NCT03298685 SAFETIM-needs : Exploring Adolescent’s and Parent’s Needs During Transition in French CF Centers https://ClinicalTrials.gov/show/NCT03298685 Completed University Hospital, Grenoble 2018-12-31
NCT03265743 HPV Vaccination in Women With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT03265743 Completed Hospices Civils de Lyon 2017-12-15
NCT03256773 High Resolution Micro OCT Imaging https://ClinicalTrials.gov/show/NCT03256773 Recruiting University of Alabama at Birmingham 2020-12-31
NCT03229213 Interactive Video Game Responses in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT03229213 Completed Pontificia Universidade Católica do Rio Grande do Sul 2019-03-31
NCT03161808 Rare CFTR Mutation Cell Collection Protocol (RARE) https://ClinicalTrials.gov/show/NCT03161808 Recruiting University of Alabama at Birmingham 2022-12-01
NCT03052283 Symptom Score to Assess Abdominal Involvement in Patients With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT03052283 Recruiting University of Jena 2020-12-31
NCT03016689 The Sinonasal Cavity as a Reservoir for Upper Airway Bacterial Development https://ClinicalTrials.gov/show/NCT03016689 Recruiting University of Minnesota 2021-01-31
NCT03001388 Longitudinal Assessment of Transient Elastography in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT03001388 Active, not recruiting National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) 2022-12-31
NCT02979340 MRI to Characterize and Predict CF Liver Disease in PUSH Cohort https://ClinicalTrials.gov/show/NCT02979340 Completed National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) 2019-12-31
NCT02958683 Chest Wall Motion Analysis in Disease https://ClinicalTrials.gov/show/NCT02958683 Completed Heart of England NHS Trust 2015-07-31
NCT02932657 Perceived Impact of Art Therapy in Patients With Cystic Fibrosis and in Professional Interdisciplinary Teams Taking Care of Them. https://ClinicalTrials.gov/show/NCT02932657 Completed Nantes University Hospital 2018-01-28
NCT02894619 Urinary and Anorectal Functional Disorders and Their Impact on CF Adults (PerineoMucoRMO) https://ClinicalTrials.gov/show/NCT02894619 Completed Fondation Ildys 2018-02-28
NCT02864446 Intestinal Fatty Acid Binding Protein in Very Low Birth Weight Infants With Meconium Obstruction https://ClinicalTrials.gov/show/NCT02864446 Completed Seoul National University Hospital 2015-09-30
NCT02853175 Lung MRI and Allergic Broncho-pulmonary Aspergillosis in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT02853175 Completed Hôpital Haut-Lévêque 2018-05-31
NCT02848560 Monitoring Response to Orkambi in Cystic Fibrosis Lung Disease by Inhaled Xenon MRI https://ClinicalTrials.gov/show/NCT02848560 Recruiting Children’s Hospital Medical Center, Cincinnati 2020-12-31
NCT02847208 Contraceptive Practices and Cervical Screening in Women With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT02847208 Completed Hospices Civils de Lyon 2014-12-31
NCT02832479 Costs of Care and Adherence to Treatment for Cystic Fibrosis https://ClinicalTrials.gov/show/NCT02832479 Completed Hospices Civils de Lyon 2016-02-29
NCT02821130 Orkambi Exercise Study https://ClinicalTrials.gov/show/NCT02821130 Active, not recruiting University of British Columbia 2019-12-31
NCT02807415 ICM to Evaluate the Activation of p.Phe508del-CFTR by Lumacaftor in Combination With Ivacaftor https://ClinicalTrials.gov/show/NCT02807415 Recruiting Hannover Medical School 2019-09-30
NCT02803944 Continuous Azithromycin in Cystic Fibrosis Patients Beyond Two Years https://ClinicalTrials.gov/show/NCT02803944 Completed Hospices Civils de Lyon 2015-09-30
NCT02797912 LBM & Lung Function in Adolescents With CF https://ClinicalTrials.gov/show/NCT02797912 Completed King’s College Hospital NHS Trust 2017-08-31
NCT02778750 Evaluation Of The Pan-microbiome and Host Immune Response in CF https://ClinicalTrials.gov/show/NCT02778750 Recruiting NYU Langone Health 2023-11-30
NCT02776098 Muscle Accrual and Function in Cystic Fibrosis-Impact of Glucose Intolerance https://ClinicalTrials.gov/show/NCT02776098 Active, not recruiting Children’s Hospital of Philadelphia 2020-12-31
NCT02722057 A Study to Confirm the Long-term Safety and Effectiveness of Kalydeco in Patients With Cystic Fibrosis Who Have an R117H-CFTR Mutation, Including Pediatric Patients https://ClinicalTrials.gov/show/NCT02722057 Completed Vertex Pharmaceuticals Incorporated 2019-12-31
NCT02710383 Biomarker for Cystic Fibrosis https://ClinicalTrials.gov/show/NCT02710383 Recruiting Centogene AG Rostock 2023-12-31
NCT02693431 Impact of Art Therapy on Anxiety Identified During Hospitalizations Among Children With Cystic Fibrosis Aged 8 to 13 https://ClinicalTrials.gov/show/NCT02693431 Completed Nantes University Hospital 2018-11-27
NCT02684422 Initial and Chronic Methicillin Resistant Staphylococcus Aureus (MRSA) Infection in Cystic Fibrosis (CF) https://ClinicalTrials.gov/show/NCT02684422 Recruiting University of North Carolina, Chapel Hill 2020-12-31
NCT02657837 Measures of Respiratory Health (MRH) https://ClinicalTrials.gov/show/NCT02657837 Recruiting The Hospital for Sick Children 2021-12-31
NCT02606487 Hyperpolarized Xenon MRI in Cystic Fibrosis Pulmonary Exacerbations https://ClinicalTrials.gov/show/NCT02606487 Completed The Hospital for Sick Children 2017-11-30
NCT00001223 Studying Patients With Cystic Fibrosis and Other Pulmonary and Pancreatic Disorders https://ClinicalTrials.gov/show/NCT00001223 Recruiting National Institutes of Health Clinical Center (CC) NA
NCT02569229 Glucose Tolerance in Children With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT02569229 Active, not recruiting University Hospital, Basel, Switzerland 2018-09-30
NCT02564393 Induction of Neutrophilic Traps ( NETs ) by the Environment and Infectious Inflammatory Lung Cystic Fibrosis https://ClinicalTrials.gov/show/NCT02564393 Completed University Hospital, Tours 2013-05-31
NCT02562911 Puberty in Girls Followed for Cystic Fibrosis https://ClinicalTrials.gov/show/NCT02562911 Completed University Hospital, Toulouse 2015-12-31
NCT03795363 Orkambi Treatment in 2 to 5 Year Old Children With CF https://ClinicalTrials.gov/show/NCT03795363 Active, not recruiting Children’s Hospital of Philadelphia 2021-06-30
NCT02558127 Asthma With Hypersecretion-associated Gene for Cystic Fibrosis https://ClinicalTrials.gov/show/NCT02558127 Completed Fundació Institut de Recerca de l’Hospital de la Santa Creu i Sant Pau 2016-02-29
NCT02555059 Special Drug Use Investigation of Ciproxan Injection in Pediatrics https://ClinicalTrials.gov/show/NCT02555059 Completed Bayer 2018-12-17
NCT02524704 Electrical Impedance Imaging of Patients With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT02524704 Completed Colorado State University 2016-12-31
NCT02480270 Outpatient Antibiotic Treatment for a Cystic Fibrosis Pulmonary Exacerbation https://ClinicalTrials.gov/show/NCT02480270 Completed University of Colorado, Denver 2017-01-04
NCT02477319 A Two-Part Multicenter Prospective Longitudinal Study of CFTR-dependent Disease Profiling in Cystic Fibrosis (PROSPECT) https://ClinicalTrials.gov/show/NCT02477319 Completed University of Alabama at Birmingham 2018-04-25
NCT02464267 Developing and Validating a Patient-reported Outcome Instrument to Monitor Symptom Management in Pulmonary Exacerbation in CF https://ClinicalTrials.gov/show/NCT02464267 Completed University of Zurich 2017-09-30
NCT02445053 Observational Study of Outcomes in Cystic Fibrosis Patients With Selected Gating Mutations on a CFTR Allele (The VOCAL Study) https://ClinicalTrials.gov/show/NCT02445053 Active, not recruiting Vertex Pharmaceuticals Incorporated 2020-12-31
NCT02417740 Natural History of Noncirrhotic Portal Hypertension https://ClinicalTrials.gov/show/NCT02417740 Recruiting National Institutes of Health Clinical Center (CC) 2029-09-04
NCT02378454 Multiple Breath Nitrogen Washout in Healthy and Cystic Fibrosis Children https://ClinicalTrials.gov/show/NCT02378454 Completed Cliniques universitaires Saint-Luc- Université Catholique de Louvain 2015-04-30
NCT02368080 Multiple Breath Nitrogen Washout in Healthy and Cystic Fibrosis Adults https://ClinicalTrials.gov/show/NCT02368080 Completed Cliniques universitaires Saint-Luc- Université Catholique de Louvain 2013-12-31
NCT02363764 The Challenge of Obtaining Qualitative Bacterial Cultures in Non-expectorating Cystic Fibrosis Patients https://ClinicalTrials.gov/show/NCT02363764 Completed Universitair Ziekenhuis Brussel 2016-08-31
NCT02305784 Kinetics of YKL-40 Protein in Serum of Cystic Fibrosis Patients https://ClinicalTrials.gov/show/NCT02305784 Completed Institut de Recherches Cliniques de Montreal 2018-06-01
NCT02288429 Evaluation of Pharmacokinetic and Pharmacodynamic Properties of Intravenous Colistimethate Sodium https://ClinicalTrials.gov/show/NCT02288429 Completed University of Colorado, Denver 2019-06-30
NCT02270476 Longitudinal Observational Study on the Course of Cystic Fibrosis Lung Disease in Patients Following Newborn Screening https://ClinicalTrials.gov/show/NCT02270476 Recruiting Heidelberg University 2021-12-31
NCT02229994 Development of a New Tool for Dyspnea Measurement in Chronic Respiratory Diseases https://ClinicalTrials.gov/show/NCT02229994 Completed Assistance Publique - Hôpitaux de Paris 2014-03-27
NCT02225899 BioEnergetics and Metabolomics in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT02225899 Completed Emory University 2018-11-07
NCT02211235 Glycemic Monitoring in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT02211235 Active, not recruiting University of Colorado, Denver 2020-12-31
NCT02203084 Social Determinants in Chronic Disease in British Columbia https://ClinicalTrials.gov/show/NCT02203084 Completed University of British Columbia 2017-06-01
NCT02198079 A Prospective, Multicenter, Collaborative Study to Determine the Prevalence of Nontuberculous Mycobacteria (NTM) in Pediatric Patients With Cystic Fibrosis in Florida https://ClinicalTrials.gov/show/NCT02198079 Completed University of Miami 2015-03-31
NCT02188758 Biomarkers of Iron Homeostasis and Responses to Cystic Fibrosis Pulmonary Exacerbation (CFPE) Treatment https://ClinicalTrials.gov/show/NCT02188758 Completed Dartmouth-Hitchcock Medical Center 2017-12-31
NCT02179710 Cystic Fibrosis Treatment Adherence Cayston Proof-of-Concept Pilot Study https://ClinicalTrials.gov/show/NCT02179710 Completed Landon Pediatric Foundation 2016-09-30
NCT02141464 Energy Balance and Weight Gain With Ivacaftor Treatment https://ClinicalTrials.gov/show/NCT02141464 Completed Children’s Hospital of Philadelphia 2016-02-29
NCT02128711 Mapping Chemical and Microbiological Heterogeneity Throughout Explanted Cystic Fibrosis Lung Specimens https://ClinicalTrials.gov/show/NCT02128711 Recruiting University of Minnesota 2020-07-31
NCT02109822 Pilot Observational Study to Determine Feasibility of a Standardized Treatment of Pulmonary Exacerb. in Patients With CF https://ClinicalTrials.gov/show/NCT02109822 Completed University of Washington 2015-06-30
NCT02073409 PREDICT Trial: PRospective Evaluation of NTM Disease In CysTic Fibrosis https://ClinicalTrials.gov/show/NCT02073409 Recruiting National Jewish Health 2023-03-31
NCT01306279 The Infective Pulmonary Exacerbations in Cystic Fibrosis - an Ecological Perspective https://ClinicalTrials.gov/show/NCT01306279 Completed Imperial College London 2012-08-31
NCT01285895 Needs in Education for Pulmonary or Cardiopulmonary Transplanted Cystic Fibrosis Patients https://ClinicalTrials.gov/show/NCT01285895 Completed Nantes University Hospital 2013-10-31
NCT01285882 Representations of Transplantation in Patients and in Health Care Professionals https://ClinicalTrials.gov/show/NCT01285882 Completed Nantes University Hospital 2012-12-31
NCT02056132 Breath Condensate Study in Patients With Cystic Fibrosis. https://ClinicalTrials.gov/show/NCT02056132 Recruiting University of Florida 2020-04-30
NCT02039986 Ivacaftor (Kalydeco) and Insulin in Cystic Fibrosis (CF) https://ClinicalTrials.gov/show/NCT02039986 Completed Children’s Hospital of Philadelphia 2016-10-11
NCT03357913 Non-respiratory Comorbidities Observed in Pulmonary French Transplant Patients With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT03357913 Completed Hospices Civils de Lyon 2017-06-01
NCT02003079 Evaluating the Impact of Chronic Rhinosinusitis on the Health-Related Quality of Life Among Adults With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT02003079 Completed St. Paul’s Hospital, Canada 2014-03-31
NCT01983787 Pharmacokinetics of Piperacillin, Given as Continuous Infusion to Patients With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT01983787 Completed University of Aarhus 2015-06-30
NCT02025829 IL-17 Neutrophils in CF Lung Inflammation https://ClinicalTrials.gov/show/NCT02025829 Completed University Hospitals Cleveland Medical Center 2014-12-31
NCT01975259 Investigating the Incretin Effect in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT01975259 Completed Liverpool Heart and Chest Hospital NHS Foundation Trust 2015-07-31
NCT01973192 Viral Pathogenesis of Early Cystic Fibrosis Lung Disease https://ClinicalTrials.gov/show/NCT01973192 Completed Indiana University 2016-12-01
NCT01931644 At-Home Research Study for Patients With Autoimmune, Inflammatory, Genetic, Hematological, Infectious, Neurological, CNS, Oncological, Respiratory, Metabolic Conditions https://ClinicalTrials.gov/show/NCT01931644 Recruiting Sanguine Biosciences 2025-08-31
NCT01883037 Comparing Laboratory Blood Glucose Results With HemoCue Glucose 201 RT https://ClinicalTrials.gov/show/NCT01883037 Completed Royal Brompton & Harefield NHS Foundation Trust 2014-04-30
NCT01863238 An Ocular Safety Study of Ivacaftor-Treated Pediatric Patients 11 Years of Age or Younger With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT01863238 Completed Vertex Pharmaceuticals Incorporated 2016-05-31
NCT01858519 Prevalence of Antibodies to Selected Porcine Viruses in Patients With Cystic Fibrosis Receiving Porcine-derived Pancreatic Enzyme Replacement Therapy https://ClinicalTrials.gov/show/NCT01858519 Completed AbbVie 2016-09-30
NCT01852448 Genetics of Insulin and Incretins in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT01852448 Active, not recruiting Children’s Hospital of Philadelphia 2024-07-31
NCT01851642 Lung Disease and Its Affect on the Work of White Blood Cells in the Lungs https://ClinicalTrials.gov/show/NCT01851642 Recruiting University of Florida 2020-09-30
NCT01848392 Extrapulmonary Effects of Cystic Fibrosis on Physical Activity of Adult Patients. https://ClinicalTrials.gov/show/NCT01848392 Completed Assistance Publique - Hôpitaux de Paris 2014-07-30
NCT01832519 Using MRI to Observe Lung Changes in Infants With CF Compared to Infants Without CF https://ClinicalTrials.gov/show/NCT01832519 Completed Children’s Hospital Medical Center, Cincinnati 2017-01-09
NCT03350828 CHaractErizing CFTR Modulated Changes in Sweat Chloride and Their Association With Clinical Outcomes https://ClinicalTrials.gov/show/NCT03350828 Recruiting Seattle Children’s Hospital 2021-01-01
NCT01815866 Cough-Generated Aerosols of NTM in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT01815866 Completed University of Florida 2015-07-31
NCT01806025 Correlation Between Haptoglobin Phenotypes and Infectious and Other Complications in Cystic Fibrosis Patients https://ClinicalTrials.gov/show/NCT01806025 Completed Carmel Medical Center 2015-01-31
NCT01799642 Evaluating Sensations of Breathlessness in Patients With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT01799642 Completed University of British Columbia 2014-12-31
NCT01736839 Detection of Reductions in Cystic Fibrosis Airway Inflammation While Using Aztreonam Lysine Solution https://ClinicalTrials.gov/show/NCT01736839 Completed National Jewish Health 2017-07-27
NCT01661491 Microbiome Acquisition and Progression of Inflammation and Airway Disease in Infants and Children With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT01661491 Recruiting Yale University 2020-12-31
NCT01652157 Long-term Study in US Cystic Fibrosis Patients Receiving Digestive Enzyme Supplements to Assess Narrowing of the Large Intestine Causing Adverse Intestinal Symptoms (Fibrosing Colonopathy) https://ClinicalTrials.gov/show/NCT01652157 Recruiting AbbVie 2022-07-29
NCT01651455 Retrospective Observational Study to Compare Cystic Fibrosis Patients in Two Decades Before and After 2000 https://ClinicalTrials.gov/show/NCT01651455 Completed Chiesi Farmaceutici S.p.A. 2013-03-31
NCT01636219 Cough Efficiency in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT01636219 Completed Sheba Medical Center 2013-06-30
NCT01626157 A Novel Assay to Quantify Treatment Response in Cystic Fibrosis (CF) https://ClinicalTrials.gov/show/NCT01626157 Completed National Jewish Health 2018-01-31
NCT01616862 The Carrier Rates of Pseudomonas Aeruginosa in Family Members of Children With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT01616862 Completed State University of New York - Upstate Medical University 2013-06-30
NCT01599052 Social Cognition in Children Treated for a Brain Tumour https://ClinicalTrials.gov/show/NCT01599052 Active, not recruiting University Medical Center Groningen 2020-12-31
NCT01572870 Duplication in CHIT1 Gene and the Risk for Aspergillus Lung Disease in CF Patients https://ClinicalTrials.gov/show/NCT01572870 Completed Rambam Health Care Campus 2011-03-31
NCT01569880 Pre-flight Evaluation of Adult Patients With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT01569880 Completed Oslo University Hospital 2008-12-31
NCT01549314 Cystic Fibrosis Related Bone Disease: the Role of CFTR https://ClinicalTrials.gov/show/NCT01549314 Completed Massachusetts General Hospital 2018-05-31
NCT01521338 G551D Observational Study- Expanded to Additional Genotypes and Extended for Long Therm Follow up (GOAL-e2) https://ClinicalTrials.gov/show/NCT01521338 Active, not recruiting University of Alabama at Birmingham 2021-01-31
NCT01479166 Bronchial Inflammation of Small Airways in Patients With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT01479166 Completed Johann Wolfgang Goethe University Hospital 2012-05-31
NCT01460836 Indirect Comparison of Tobramycin Solution for Inhalation Versus Aztreonam Lysine for Inhalation in the Treatment of Cystic Fibrosis https://ClinicalTrials.gov/show/NCT01460836 Completed Novartis 2010-10-31
NCT01424696 Baby Observational and Nutritional Study https://ClinicalTrials.gov/show/NCT01424696 Completed Seattle Children’s Hospital 2015-04-30
NCT01401998 UAB HRFD Core Center: Core A: The Hepato/Renal Fibrocystic Diseases Translational Resource https://ClinicalTrials.gov/show/NCT01401998 Recruiting Children’s National Research Institute 2022-09-30
NCT01401439 Assessment of Fat Free Mass Index and Its Impact on Health in Children With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT01401439 Completed University of Arkansas 2016-07-31
NCT01375036 Registry to Monitor the Susceptibility to Aztreonam of Pseudomonas Aeruginosa Isolates From Cystic Fibrosis Patients https://ClinicalTrials.gov/show/NCT01375036 Completed Gilead Sciences 2016-12-31
NCT01353950 Costimulatory Molecules as Biomarkers in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT01353950 Completed Oregon Health and Science University 2013-06-30
NCT01345617 A Study of Sweat Testing Using a Quantitative Patch https://ClinicalTrials.gov/show/NCT01345617 Completed Polychrome Medical, Inc. 2013-10-31
NCT01343524 Changes in Lung Function Based on Differences in Spirometry Equipment Used in Children With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT01343524 Completed State University of New York - Upstate Medical University 2010-12-31
NCT01331980 Bone Microarchitecture at the Radius: a Pilot Comparison Between Children With Cystic Fibrosis and Healthy Controls https://ClinicalTrials.gov/show/NCT01331980 Completed University of Arkansas 2015-07-31
NCT04400955 A Study of Web and Tablet-based Interactive Audiometry in Adults With CF https://ClinicalTrials.gov/show/NCT04400955 Completed Royal Brompton & Harefield NHS Foundation Trust 2019-03-01
NCT04397861 T Cell Memory Fuels the Innate Response in Chronic CF Lung Disease https://ClinicalTrials.gov/show/NCT04397861 Active, not recruiting National Jewish Health 2019-05-01
NCT04397809 Utility of CD64 and TLR2 Assays to Diagnose Acute Pulmonary Exacerbations in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT04397809 Active, not recruiting National Jewish Health 2019-05-23
NCT04392544 Intestinal Inflammation in CF Patients https://ClinicalTrials.gov/show/NCT04392544 Recruiting The Hospital for Sick Children 2021-03-31
NCT04354038 Host and Bacterial Mechanisms During Cystic Fibrosis Pulmonary Exacerbations https://ClinicalTrials.gov/show/NCT04354038 Recruiting National Jewish Health 2025-12-31
NCT04341532 Bacterial Gene Profiling to Predict Antibiotic Resistance During Cystic Fibrosis Pulmonary Exacerbations https://ClinicalTrials.gov/show/NCT04341532 Recruiting National Jewish Health 2023-12-31
NCT04302428 Zinc Status and Growth in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT04302428 Recruiting Indiana University 2021-06-30
NCT04301856 Response to CFTR Modulators in CF Patients Under 18 Years https://ClinicalTrials.gov/show/NCT04301856 Recruiting Societe Francaise de la Mucoviscidose 2025-07-01
NCT04256772 Anti-IL5 and Other Biotherapies in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT04256772 Recruiting University Hospital, Montpellier 2020-06-01
NCT04225962 Intimacy of Women With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT04225962 Recruiting Hospices Civils de Lyon 2020-11-30
NCT04206436 CFTR Modulator Effects on Bone and Muscle in Adults With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT04206436 Enrolling by invitation Indiana University 2022-10-01
NCT04217889 Cystic Fibrosis Adherence Study https://ClinicalTrials.gov/show/NCT04217889 Recruiting Hospices Civils de Lyon 2020-07-31
NCT04174664 Comparison of Different Functional Capacity Tests in Cystic Fibrosis Patients With Acute Pulmonary Exacerbation https://ClinicalTrials.gov/show/NCT04174664 Recruiting Hacettepe University 2021-01-01
NCT04171583 Mucoid Staphylococcus Aureus in Cystic Fibrosis Airways https://ClinicalTrials.gov/show/NCT04171583 Recruiting University Hospital Muenster 2020-05-31
NCT04161313 Respiratory Function, Exercise Capacity and Peripheral Muscle Strength Among Patients With CF, PCD and Healthy Children https://ClinicalTrials.gov/show/NCT04161313 Completed Bezmialem Vakif University 2020-02-24
NCT04157361 Pulmonary Condensate: Non-invasive Evaluation of Pulmonary Involvement in Asthma and Cystic Fibrosis. https://ClinicalTrials.gov/show/NCT04157361 Recruiting The Institute of Molecular and Translational Medicine, Czech Republic 2020-01-31
NCT04138589 Effect of Lumacaftor/Ivacaftor in Children With Cystic Fibrosis Homozygote for F508del on Small Airway Function https://ClinicalTrials.gov/show/NCT04138589 Recruiting University Medical Center Groningen 2021-02-01
NCT04071314 Evaluating the Alimentary and Respiratory Tracts in Health and Disease (EARTH) Research Program. https://ClinicalTrials.gov/show/NCT04071314 Recruiting The University of New South Wales 2023-03-13
NCT04056702 Impact of Triple Combination CFTR Therapy on Sinus Disease. https://ClinicalTrials.gov/show/NCT04056702 Active, not recruiting National Jewish Health 2021-04-30
NCT04038710 Clinical Outcomes of Triple Combination Therapy in Severe Cystic Fibrosis Disease. https://ClinicalTrials.gov/show/NCT04038710 Active, not recruiting National Jewish Health 2021-02-28
NCT04038047 A Prospective Study to Evaluate Biological and Clinical Effects of Significantly Corrected CFTR Function https://ClinicalTrials.gov/show/NCT04038047 Active, not recruiting Seattle Children’s Hospital 2022-11-30
NCT04026360 Impact of Early Lung Physiology, Viral Infections and the Microbiota on the Development and Progression of Lung Disease in Children With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT04026360 Recruiting University Hospital Inselspital, Berne 2050-08-31
NCT04024423 Healthcare-associated Links in Transmission of Nontuberculous Mycobacteria in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT04024423 Recruiting National Jewish Health 2021-07-01
NCT04016571 Parameters to Assess Response to Intra-Venous Antibiotic Treatment for Pulmonary Exacerbations in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT04016571 Recruiting Belfast Health and Social Care Trust 2019-09-30
NCT04016194 Prediction of Survival in Children With Cystic Fibrosis Using the Multiple-breath Washout https://ClinicalTrials.gov/show/NCT04016194 Completed University Hospital Inselspital, Berne 2005-12-31
NCT03961516 Glycemic Characterization and Pancreatic Imaging Correlates in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT03961516 Recruiting University Hospitals Cleveland Medical Center 2020-07-01
NCT03910920 Cross Transmissions of Pseudomonas Aeruginosa Between Children From a Same Cystic Fibrosis Center. https://ClinicalTrials.gov/show/NCT03910920 Enrolling by invitation Queen Fabiola Children’s University Hospital 2021-01-31
NCT03902236 Reaction Time and Postural Control in Individuals With Cystic Fibrosis and Bronchiectasis https://ClinicalTrials.gov/show/NCT03902236 Recruiting Hacettepe University 2019-10-07
NCT03892304 Gynecological Health Improvement of Adult Women With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT03892304 Completed Hospices Civils de Lyon 2017-12-31
NCT03886350 Implication of UNconventionaL T Lymphocytes in Cystic Fibrosis (UNLOCk) https://ClinicalTrials.gov/show/NCT03886350 Recruiting University Hospital, Tours 2022-04-30
NCT03859531 Gastrointestinal Study at Orkambi Therapy in CF Patients https://ClinicalTrials.gov/show/NCT03859531 Recruiting Karolinska University Hospital 2020-06-30
NCT03853629 Air Pollution and Children With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT03853629 Completed Queen Mary University of London 2020-01-30
NCT03850145 Educational Program Through Video Conference for Inhaled Therapies in Cystic Fibrosis Patients https://ClinicalTrials.gov/show/NCT03850145 Completed University Hospital, Montpellier 2019-12-01
NCT03839992 Detection of Unsuspected Small Airways Obstruction in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT03839992 Recruiting Gelb, Arthur F., M.D. 2020-04-25
NCT03801993 Multicenter Study of Patient-reported Gastrointestinal Symptoms in People With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT03801993 Completed Seattle Children’s Hospital 2019-09-17
NCT03754088 In Vitro Model of the Cystic Fibrosis Bronchial Epithelium Via iPS Technology https://ClinicalTrials.gov/show/NCT03754088 Completed University Hospital, Montpellier 2019-04-25
NCT03753828 Estimated Impact of Fungal Colonization in Cystic Fibrosis From Secondary Exploitation of MucoFong Database. https://ClinicalTrials.gov/show/NCT03753828 Completed University Hospital, Bordeaux 2018-10-13
NCT03736096 Molecular Diagnosis of Respiratory Viral Infections on Sputum From Cystic Fibrosis Patients https://ClinicalTrials.gov/show/NCT03736096 Recruiting University Hospital, Brest 2019-10-31
NCT03728595 Validation of a Predictive Score for HAST https://ClinicalTrials.gov/show/NCT03728595 Recruiting The Leeds Teaching Hospitals NHS Trust 2021-07-31
NCT03713437 Measurement of Beta Cell Death in Individuals With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT03713437 Recruiting University of Nebraska 2020-06-30
NCT03674216 Study of Peripherally Inserted Venous Catheters in Cystic Fibrosis Patients https://ClinicalTrials.gov/show/NCT03674216 Recruiting Maine Medical Center 2021-12-31
NCT03670472 Correction of Nonsense Mutations in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT03670472 Recruiting University Hospital, Lille 2028-01-31
NCT03659214 Impact of the Introduction of ORKAMBI on Anxiety, Depression, Quality of Life and Adherence of Adolescents and Young Adults https://ClinicalTrials.gov/show/NCT03659214 Recruiting Assistance Publique - Hôpitaux de Paris 2018-12-31
NCT03652090 Primary Nasal Cell Culture as a Tool for Personalized Therapy in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT03652090 Completed Institut National de la Santé Et de la Recherche Médicale, France 2016-03-03
NCT03684759 Sputum Validation for the Molecular Diagnosis of Respiratory Viral Infections in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT03684759 Completed University Hospital, Brest 2017-02-06
NCT03607396 Study for Evaluating the Real Use of Inhaled Aztreonam Lysine in Patients With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT03607396 Recruiting Hospital Universitari Vall d’Hebron Research Institute 2019-07-01
NCT03593434 Airway Clearance Therapy on Hyperpolarized 129Xenon and MRI https://ClinicalTrials.gov/show/NCT03593434 Recruiting Children’s Hospital Medical Center, Cincinnati 2020-07-30
NCT03579173 Determinants of Early Cystic Fibrosis Lung Disease https://ClinicalTrials.gov/show/NCT03579173 Active, not recruiting Indiana University 2020-04-30
NCT03569904 Markers of Pulmonary Dysbiosis Associated With Exacerbation in Patients Followed for Cystic Fibrosis https://ClinicalTrials.gov/show/NCT03569904 Recruiting University Hospital, Grenoble 2021-09-30
NCT03566550 Gut Imaging for Function & Transit in Cystic Fibrosis Study 1 https://ClinicalTrials.gov/show/NCT03566550 Completed Nottingham University Hospitals NHS Trust 2019-02-20
NCT03565692 Lum-Iva-biota: Exploring the Respiratory Mycobiota and Microbiota Profile in French CF Patients Taking Lumacaftor-Ivacaftor https://ClinicalTrials.gov/show/NCT03565692 Recruiting University Hospital, Bordeaux 2023-02-28
NCT03524859 Evaluation of Sit-to-stand Test in Patients With Cystic Fibrosis and Matched Controls. https://ClinicalTrials.gov/show/NCT03524859 Completed Universidad Católica San Antonio de Murcia 2019-03-26
NCT03513640 Risk Factors of Meconium Obstruction and Respiratory Distress Syndrome in Preterm Infants https://ClinicalTrials.gov/show/NCT03513640 Recruiting Seoul National University Hospital 2021-04-30
NCT03512119 Observational Study of Glucose Tolerance Abnormalities in Patient With Cystic Fibrosis Homozygous for Phe 508 Del CFTR Treated by Lumacaftor-Ivacaftor https://ClinicalTrials.gov/show/NCT03512119 Completed University Hospital, Strasbourg, France 2018-04-30
NCT03494894 Bacteriological Link Between Upper and Lower Airways in Cystic Fibrosis and Primary Ciliary Dyskinesia https://ClinicalTrials.gov/show/NCT03494894 Recruiting Centre Hospitalier Intercommunal Creteil 2019-09-01
NCT03445793 : TRANSITION: An Observational Study of Transition From Lumacaftor/Ivacaftor to Tezacaftor/Ivacaftor (Tez/Iva) https://ClinicalTrials.gov/show/NCT03445793 Completed National Jewish Health 2019-11-01
NCT03437811 Airway Clearance System (K031876) Phase IV Device Efficacy https://ClinicalTrials.gov/show/NCT03437811 Completed Mack Biotech, Corp. 2019-11-01
NCT01241890 Prevention of CF Exacerbation in Childhood: PREVEC Study https://ClinicalTrials.gov/show/NCT01241890 Completed Maastricht University Medical Center 2013-08-31
NCT01238081 The Role of Respiratory Viruses in Exacerbations of Cystic Fibrosis in Adults https://ClinicalTrials.gov/show/NCT01238081 Completed Manchester University NHS Foundation Trust 2012-04-30
NCT01150136 Choline Nutritional Status Of Children With Cystic Fibrosis X-Sectional Study https://ClinicalTrials.gov/show/NCT01150136 Completed University of British Columbia 2009-03-31
NCT01144507 Prediction by Ultrasound of the Risk of Hepatic Cirrhosis in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT01144507 Active, not recruiting National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) 2022-11-30
NCT01116414 Molecular Phenotypes for Cystic Fibrosis Lung Disease https://ClinicalTrials.gov/show/NCT01116414 Enrolling by invitation University of North Carolina, Chapel Hill 2020-04-30
NCT01113216 Genetic Modifiers of Cystic Fibrosis Related Diabetes https://ClinicalTrials.gov/show/NCT01113216 Enrolling by invitation Johns Hopkins University 2025-04-30
NCT01078740 Detection of Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) Activity in Rectal Tissues From Human Subjects https://ClinicalTrials.gov/show/NCT01078740 Completed CF Therapeutics Development Network Coordinating Center 2010-07-31
NCT00943514 Natural History of Bronchiectasis https://ClinicalTrials.gov/show/NCT00943514 Recruiting National Institutes of Health Clinical Center (CC) NA
NCT00908830 Effects of Mycophenolate Mofetil in Cystic Fibrosis Lung Transplant Patients https://ClinicalTrials.gov/show/NCT00908830 Completed University of Michigan 2011-05-31
NCT00906568 Evaluation of Bronchial Inflammation in Allergic Bronchopulmonary Aspergillosis (ABPA) https://ClinicalTrials.gov/show/NCT00906568 Completed Johann Wolfgang Goethe University Hospital 2010-05-31
NCT00863694 Fecal Calprotectin in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT00863694 Completed Medical College of Wisconsin 2013-08-31
NCT04353752 Observational Trial of the Longitudinal Effects of CFTR Modulator Drugs https://ClinicalTrials.gov/show/NCT04353752 Recruiting National Jewish Health 2023-12-31
NCT04335370 Pharmacokinetics of Polymyxin B in Adult Patients With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT04335370 Recruiting University of Michigan 2020-12-31
NCT04297709 Study of Urinary Predictors of Exacerbations by Biomarkers in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT04297709 Completed Mologic Ltd 2019-07-31
NCT03783286 Ivacaftor Treatment in 6 Month to 2 Year Old CF Subjects https://ClinicalTrials.gov/show/NCT03783286 Active, not recruiting Children’s Hospital of Philadelphia 2020-06-01
NCT03622892 Non-invasive Prenatal Diagnosis of Monogenic Disorders by Linked-reads Technology https://ClinicalTrials.gov/show/NCT03622892 Recruiting University Hospital, Brest 2021-10-18
NCT02194881 Ivacaftor in French Patients With Cystic Fibrosis and a G551D Mutation https://ClinicalTrials.gov/show/NCT02194881 Completed Assistance Publique - Hôpitaux de Paris 2016-02-29
NCT03919604 ECMO for Lung Transplantation in Cystic Fibrosis Patients https://ClinicalTrials.gov/show/NCT03919604 Completed Policlinico Hospital 2018-12-31
NCT03234387 A CFit Study - Baseline https://ClinicalTrials.gov/show/NCT03234387 Recruiting University of Portsmouth 2020-03-31
NCT01533636 CF And Effects of Drugs Mixed Ex Vivo With Sputum for Mucolytic Treatment https://ClinicalTrials.gov/show/NCT01533636 Recruiting University of California, San Francisco 2020-04-30
NCT01379040 Volatile Organic Compounds in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT01379040 Completed Landon Pediatric Foundation 2009-12-31
NCT01319253 A Comparator Study Evaluating Microbiological Resistance and Effects of Alternating Inhaled Antibiotic Therapies https://ClinicalTrials.gov/show/NCT01319253 Completed Indiana University 2012-07-31
NCT00806455 Exercise-Induced Bronchospasm in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT00806455 Completed Ohio State University 2013-08-31
NCT00804661 Sleep in Patients With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT00804661 Completed Assistance Publique - Hôpitaux de Paris 2009-06-30
NCT00804583 Genetic Modifiers of Cystic Fibrosis (CF) Liver Disease https://ClinicalTrials.gov/show/NCT00804583 Active, not recruiting University of North Carolina, Chapel Hill 2021-07-31
NCT00368446 Genetic Disorders of Mucociliary Clearance in Nontuberculous Mycobacterial Lung Disease https://ClinicalTrials.gov/show/NCT00368446 Completed National Institutes of Health Clinical Center (CC) NA
NCT02419989 PATIENCE Trial: Prospective Algorithm for Treatment of NTM in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT02419989 Recruiting National Jewish Health 2023-03-31
NCT01805713 Biomarkers of Injury and Destruction in the Cystic Fibrosis Lung https://ClinicalTrials.gov/show/NCT01805713 Completed University of Minnesota 2017-12-31
NCT01488721 Clinical Evaluation of NeoPlex4 Assay and NeoPlex System https://ClinicalTrials.gov/show/NCT01488721 Completed Luminex Molecular Diagnostics 2012-02-29
NCT04402801 Patient Outcomes of Clinic Transition From Face to Face Encounter to Telemedicine in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT04402801 Enrolling by invitation University of Virginia 2021-05-31
NCT04306939 Genomic Resources for Enhancing Available Therapies (GREAT1.0) Study https://ClinicalTrials.gov/show/NCT04306939 Recruiting University of Pittsburgh 2025-12-01
NCT00834054 Measurement of Lung Water by Transpulmonary Thermodilution in Lung Transplanted Patients https://ClinicalTrials.gov/show/NCT00834054 Completed Hopital Foch 2011-07-31
NCT00788359 Cystic Fibrosis Foundation (CFF) Biomarkers of Exacerbation https://ClinicalTrials.gov/show/NCT00788359 Completed University of Colorado, Denver 2012-07-31
NCT00779077 Cystic Fibrosis (CF) Flow Rates Study https://ClinicalTrials.gov/show/NCT00779077 Completed Pharmaxis 2009-02-28
NCT00760071 Magnetic Resonance Imaging (MRI) for Early Diagnosis of Cystic Fibrosis (CF) https://ClinicalTrials.gov/show/NCT00760071 Completed German Cancer Research Center 2008-10-31
NCT00758771 Using Rheological Methods to Characterize Cystic Fibrosis (CF) Sputum and the Effects of Mucoactive Agents https://ClinicalTrials.gov/show/NCT00758771 Completed University of California, San Francisco 2012-12-31
NCT00750932 Biodistribution of Neutrophile Proteases in the Sputum of Patients Affected by Cystic Fibrosis https://ClinicalTrials.gov/show/NCT00750932 Completed University Hospital, Tours 2012-01-31
NCT00727285 Cystic Fibrosis (CF) Leukocyte Genes as Biomarkers for Novel Therapies https://ClinicalTrials.gov/show/NCT00727285 Completed National Jewish Health 2011-10-31
NCT00676169 The EPIC Observational Study https://ClinicalTrials.gov/show/NCT00676169 Completed CF Therapeutics Development Network Coordinating Center 2018-12-31
NCT00670579 Study About Complications of Totally Implanted Venous Access Devices (TIVADs) in People With Cystic Fibrosis (CF) https://ClinicalTrials.gov/show/NCT00670579 Completed University of Florence 2009-10-31
NCT00669760 Dissection of Staphylococcus Aureus Infection From Colonization in Cystic Fibrosis Patients https://ClinicalTrials.gov/show/NCT00669760 Completed University Hospital Muenster 2011-07-31
NCT00596232 Investigating Mucinase Activity in Airway Disease https://ClinicalTrials.gov/show/NCT00596232 Completed University of California, San Francisco 2015-12-31
NCT00590330 Microbial Community Composition and Dynamics in Lungs of Cystic Fibrosis Sibling Pairs https://ClinicalTrials.gov/show/NCT00590330 Completed Boston Children’s Hospital 2009-03-31
NCT00585364 Mechanisms of Immune Tolerance and Inflammation in Patients With Cystic Fibrosis With ABPA https://ClinicalTrials.gov/show/NCT00585364 Completed University of Pittsburgh 2010-12-31
NCT00577252 Coping Compliance and Adjustment in Adolescents With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT00577252 Completed Akron Children’s Hospital NA
NCT00531531 Evaluation of the Emission Distance of P. Aeruginosa From the Respiratory Tract of People With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT00531531 Completed University of Florence 2008-08-31
NCT00504361 Blood Collection From Individuals With Lung Disease for Genetic Studies (Qatar) https://ClinicalTrials.gov/show/NCT00504361 Completed Weill Medical College of Cornell University 2012-05-31
NCT00485082 Disclosing a Cystic Fibrosis Diagnosis to a Dating Partner https://ClinicalTrials.gov/show/NCT00485082 Completed National Institutes of Health Clinical Center (CC) 2008-03-21
NCT00457301 Using Health-related Quality of Life (HRQL) in Routine Clinical Care https://ClinicalTrials.gov/show/NCT00457301 Completed University of Alberta 2007-04-30
NCT00413140 Non-Invasive Biomarkers in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT00413140 Completed Maastricht University Medical Center NA
NCT00381628 Nasal Epithelial Cells/Blood Lymphocyte Markers for Cystic Fibrosis (CF)/CF Pulmonary Exacerbations https://ClinicalTrials.gov/show/NCT00381628 Completed University Hospitals Cleveland Medical Center 2011-09-30
NCT00362739 Blood Collection From Individuals With Lung Disease for Genetic Studies https://ClinicalTrials.gov/show/NCT00362739 Completed Weill Medical College of Cornell University 2015-08-31
NCT00360503 Antimicrobial Resistance in Cystic Fibrosis (CF) https://ClinicalTrials.gov/show/NCT00360503 Completed Seattle Children’s Hospital NA
NCT00333957 Capsule Endoscopy in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT00333957 Completed Hadassah Medical Organization NA
NCT00323167 Rare Genetic Disorders of the Breathing Airways https://ClinicalTrials.gov/show/NCT00323167 Completed University of North Carolina, Chapel Hill 2012-10-31
NCT00311506 A Study to Determine the Variability of a 6-Minute Walk Test in Cystic Fibrosis Subjects With Advanced Lung Disease https://ClinicalTrials.gov/show/NCT00311506 Completed Genentech, Inc. 2004-06-30
NCT00266474 Prevalence of Chronic Rhinosinusitis in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT00266474 Completed University of Jena NA
NCT00222508 The Microvascular Complications Study https://ClinicalTrials.gov/show/NCT00222508 Completed University of Minnesota NA
NCT00221559 Serum Zn Status of Patients With Cystic Fibrosis at Diagnosis and One Year Later, Compared to a Healthy Control Group https://ClinicalTrials.gov/show/NCT00221559 Completed University Hospital, Ghent NA
NCT00043225 The Role of Bacteria and Genetic Variations in Cystic Fibrosis https://ClinicalTrials.gov/show/NCT00043225 Completed National Institutes of Health Clinical Center (CC) NA
NCT00037778 Genetic Modifiers of Cystic Fibrosis: Sibling Study https://ClinicalTrials.gov/show/NCT00037778 Completed Johns Hopkins University 2013-02-28
NCT00037765 Gene Modifiers of Cystic Fibrosis Lung Disease https://ClinicalTrials.gov/show/NCT00037765 Active, not recruiting University of North Carolina, Chapel Hill 2021-07-31
NCT00027183 Role of Toxins in Lung Infections Caused by Pseudomonas Aeruginosa https://ClinicalTrials.gov/show/NCT00027183 Completed National Institutes of Health Clinical Center (CC) NA
NCT00404859 FLAME: Airway Inflammation Monitoring in Asthma and Cystic Fibrosis https://ClinicalTrials.gov/show/NCT00404859 Completed Maastricht University Medical Center NA
NCT00015756 Tissue Collection From People With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT00015756 Completed National Institutes of Health Clinical Center (CC) NA
NCT00014781 Study of Hepatic Glucose Production and De Novo Lipogenesis in Patients With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT00014781 Completed Office of Rare Diseases (ORD) NA
NCT00008762 Bone Health of People With Cystic Fibrosis https://ClinicalTrials.gov/show/NCT00008762 Completed National Center for Research Resources (NCRR) NA
NCT00004296 Multicenter Study of Nontuberculous Mycobacteria in Cystic Fibrosis Patients https://ClinicalTrials.gov/show/NCT00004296 Completed Office of Rare Diseases (ORD) NA

Registries

#If less then 500 registries

nct_id brief_title link overall_status source primary_completion_date
NCT02907788 Inflammatory Markers in Broncho-alveolar Lavage Fluid as Risk Factors for Lung Disease in Infants With Cystic Fibrosis: the I-BALL Study https://ClinicalTrials.gov/show/NCT02907788 Recruiting Erasmus Medical Center 2022-12-31
NCT02449031 Observational Study in Cystic Fibrosis Patients Using TOBI® Podhaler™ or Other FDA Approved Inhaled Antipseudomonal Antibacterial Drugs https://ClinicalTrials.gov/show/NCT02449031 Active, not recruiting Mylan Inc. 2023-07-31
NCT02309229 Sputum Purulence as a Predictor of Cystic Fibrosis Exacerbations: a Prospective Cohort Trial. https://ClinicalTrials.gov/show/NCT02309229 Completed Universitaire Ziekenhuizen Leuven 2013-12-31
NCT02043717 Increased Vitamin D Reduces Pulmonary Exacerbations in CF https://ClinicalTrials.gov/show/NCT02043717 Completed Hadassah Medical Organization 2015-01-31
NCT04277819 The Use of Novel Diagnostic Tools to Increase Detection of Early Fibrosis in Cystic Fibrosis Related Liver Disease to Improve Clinical Management https://ClinicalTrials.gov/show/NCT04277819 Recruiting Manchester University NHS Foundation Trust 2020-08-30
NCT04259983 Investigation of Relationship Between Vascular Functions, Exercise Capacity, and Respiratory Functions in CF https://ClinicalTrials.gov/show/NCT04259983 Active, not recruiting Hacettepe University 2022-01-08
NCT03809091 WGS of Korean Idiopathic Bronchiectasis https://ClinicalTrials.gov/show/NCT03809091 Recruiting Seoul National University Hospital 2021-08-31